Optician Online1 小时
Stargardt eye disease trial begins
SpliceBio, a clinical-stage genetic medicines company, announced that it has dosed the first patient in the phase ½ Astra ...
Gene editing with adeno-associated virus vector offers hope for hereditary deafness
An R75W mutation in the gap junction β2 (GJB2) gene causes severe fragmentation of gap junction plaques, connecting adjacent ...
Gene therapy reverses symptoms of rare neurological disease in animal models
A recent study led by the UAB demonstrates the potential of gene therapy to restore motor capacity in an ultra-rare disease, ...
Detailed atlas identifies optimal viral vectors for precise gene therapy
Gene therapy, a technique that is revolutionizing the treatment of multiple genetic conditions, including eye and muscle diseases and blood disorders, requires efficient and specific delivery of the ...
Technology Networks2 天
Gene Therapy Restores Motor Capacity in Animal Models of Rare Neurological Disease
A recent study demonstrated the potential of gene therapy to restore motor capacity in an ultra-rare disease, megalencephalic ...
GEN - Genetic Engineering and Biotechnology News20 小时
Digital Twin Focuses on Improving Viral Vector Production
The combination of synchronous experimental process development and digital twin core model development is among the first of its kind.
The American Journal of Managed Care18 小时
The Value of Newborn Screening for DMD: Barry Byrne, MD, PhD
Barry Byrne, MD, PhD, Powell Gene Therapy Center at the University of Florida, discusses gene therapy considerations for pediatric patients and how newborn screening can influence outcomes for ...
Mirage News3 天
Gene Therapy Reverses Rare Neurological Disease In Animals
A recent study led by the UAB demonstrates the potential of gene therapy to restore motor capacity in an ultra-rare disease, ...
Taiwan News13 天
OXB honoured at 2025 CDMO Leadership Awards in 'Cell & Gene Therapy – Global' category
Oxford, UK – 21 March 2025: OXB (LSE: OXB) (the "Company"), a quality and innovation-led cell and gene therapy CDMO, today announces that the Company has been recognised as a winner in the 'Cell & ...